About 500 reports

Global Genetic Disorders Partnering 2014 to 2021 provides the full collection of Genetic Disorders disease deals signed between the world’s pharmaceutical and biotechnology companies since 2014. Trends in Genetic Disorders partnering deals Financial deal terms for headline, upfront and royalty by stage of development Genetic...

  • Genetic Disorder
  • World

Achromatopsia (Genetic Disorders) - Drugs in Development, 2021 Summary Achromatopsia (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Achromatopsia pipeline landscape. The report provides comprehensive information on the therapeutics under development for Achromatopsia,...

  • Genetic Disorder
  • Eye Disease
  • World

Cystinuria (Genetic Disorders) - Drugs in Development, 2021 Summary Cystinuria (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Cystinuria pipeline landscape. The report provides comprehensive information on the therapeutics under development for Cystinuria, complete...

  • Genetic Disorder
  • World

Turner Syndrome (Genetic Disorders) - Drugs in Development, 2021 Summary Turner Syndrome (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Turner Syndrome pipeline landscape. The report provides comprehensive information on the therapeutics under development for...

  • Genetic Disorder
  • World

Barth Syndrome (Genetic Disorders) - Drugs in Development, 2021 Summary Barth Syndrome (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Barth Syndrome pipeline landscape. The report provides comprehensive information on the therapeutics under development for Barth...

  • Genetic Disorder
  • Neurological Disorder
  • World

Congenital Ichthyosis (Genetic Disorders) - Drugs in Development, 2021 Summary Congenital Ichthyosis (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Congenital Ichthyosis pipeline landscape. The report provides comprehensive information on the therapeutics under...

  • Genetic Disorder
  • Dermatological Condition
  • World

Alport Syndrome (Genetic Disorders) - Drugs in Development, 2021 Summary Alport Syndrome (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Alport Syndrome pipeline landscape. The report provides comprehensive information on the therapeutics under development for...

  • Genetic Disorder
  • World

Ichthyosis Vulgaris (Genetic Disorders) - Drugs in Development, 2021 Summary Ichthyosis Vulgaris (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Ichthyosis Vulgaris pipeline landscape. The report provides comprehensive information on the therapeutics under development...

  • Genetic Disorder
  • Dermatological Condition
  • World

Tuberous Sclerosis (Genetic Disorders) - Drugs in Development, 2021 Summary Tuberous Sclerosis (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Tuberous Sclerosis pipeline landscape. The report provides comprehensive information on the therapeutics under development...

  • Genetic Disorder
  • Neurological Disorder
  • World

Angelman Syndrome (Genetic Disorders) - Drugs in Development, 2021 Summary Angelman Syndrome (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Angelman Syndrome pipeline landscape. The report provides comprehensive information on the therapeutics under development...

  • Genetic Disorder
  • Neurological Disorder
  • World

Chronic Granulomatous Disease (Genetic Disorders) - Drugs in Development, 2021 Summary Chronic Granulomatous Disease (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Chronic Granulomatous Disease pipeline landscape. The report provides comprehensive information...

  • Genetic Disorder
  • World

Hutchinson-Gilford Progeria (Genetic Disorders) - Drugs in Development, 2021 Summary Hutchinson-Gilford Progeria (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Hutchinson-Gilford Progeria pipeline landscape. The report provides comprehensive information on the...

  • Genetic Disorder
  • World

Urea Cycle Disorders (Genetic Disorders) - Drugs in Development, 2021 Summary Urea Cycle Disorders (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Urea Cycle Disorders pipeline landscape. The report provides comprehensive information on the therapeutics under development...

  • Genetic Disorder
  • World

Inherited Mitochondrial Disorders (Genetic Disorders) - Drugs in Development, 2021 Summary Inherited Mitochondrial Disorders (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Inherited Mitochondrial Disorders pipeline landscape. The report provides comprehensive...

  • Genetic Disorder
  • World

X-Linked SCID (Genetic Disorders) - Drugs in Development, 2021 Summary X-Linked SCID (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the X-Linked SCID pipeline landscape. The report provides comprehensive information on the therapeutics under development for X-Linked...

  • Genetic Disorder
  • World

Inherited Metabolic Disorders (Genetic Disorders) - Drugs in Development, 2021 Summary Inherited Metabolic Disorders (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Inherited Metabolic Disorders pipeline landscape. The report provides comprehensive information...

  • Endocrine Disease
  • Genetic Disorder
  • World

Tay-Sachs Disease (Genetic Disorders) - Drugs in Development, 2021 Summary Tay-Sachs Disease (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Tay-Sachs Disease pipeline landscape. The report provides comprehensive information on the therapeutics under development...

  • Genetic Disorder
  • Neurological Disorder
  • World

Charcot-Marie-Tooth Disease (Genetic Disorders) - Drugs in Development, 2021 Summary Charcot-Marie-Tooth Disease (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Charcot-Marie-Tooth Disease pipeline landscape. The report provides comprehensive information on the...

  • Genetic Disorder
  • World

Gaucher Disease Type II (Genetic Disorders) - Drugs in Development, 2021 Summary Gaucher Disease Type II (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Gaucher Disease Type II pipeline landscape. The report provides comprehensive information on the therapeutics...

  • Genetic Disorder
  • World

Maple Syrup Urine Disease (Genetic Disorders) - Drugs in Development, 2021 Summary Maple Syrup Urine Disease (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Maple Syrup Urine Disease pipeline landscape. The report provides comprehensive information on the therapeutics...

  • Genetic Disorder
  • World

Aicardi-Goutieres Syndrome (AGS) (Genetic Disorders) - Drugs in Development, 2021 Summary Aicardi-Goutieres Syndrome (AGS) (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Aicardi-Goutieres Syndrome (AGS) pipeline landscape. The report provides comprehensive information...

  • Genetic Disorder
  • World

Amino Acid Metabolism Disorders (Genetic Disorders) - Drugs in Development, 2021 Summary Amino Acid Metabolism Disorders (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Amino Acid Metabolism Disorders pipeline landscape. The report provides comprehensive information...

  • Genetic Disorder
  • Endocrine Disease
  • World

Hyperargininemia (Arginase I Deficiency) (Genetic Disorders) - Drugs in Development, 2021 Summary Hyperargininemia (Arginase I Deficiency) (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Hyperargininemia (Arginase I Deficiency) pipeline landscape. The report provides...

  • Genetic Disorder
  • World

Glycogen Storage Disorders (GSD) (Genetic Disorders) - Drugs in Development, 2021 Summary Glycogen Storage Disorders (GSD) (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Glycogen Storage Disorders (GSD) pipeline landscape. The report provides comprehensive information...

  • Genetic Disorder
  • World

Glycogen Storage Disease 1A (Genetic Disorders) - Drugs in Development, 2021 Summary Glycogen Storage Disease 1A (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Glycogen Storage Disease 1A pipeline landscape. The report provides comprehensive information on the...

  • Endocrine Disease
  • Genetic Disorder
  • World

Gaucher Disease Type III (Genetic Disorders) - Drugs in Development, 2021 Summary Gaucher Disease Type III (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Gaucher Disease Type III pipeline landscape. The report provides comprehensive information on the therapeutics...

  • Genetic Disorder
  • World

Gaucher Disease Type I (Genetic Disorders) - Drugs in Development, 2021 Summary Gaucher Disease Type I (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Gaucher Disease Type I pipeline landscape. The report provides comprehensive information on the therapeutics under...

  • Genetic Disorder
  • World

Severe Combined Immune Deficiency (SCID) (Genetic Disorders) - Drugs in Development, 2021 Summary Severe Combined Immune Deficiency (SCID) (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Severe Combined Immune Deficiency (SCID) pipeline landscape. The report provides...

  • Genetic Disorder
  • World

Subacute Necrotizing Encephalomyelopathy (Leigh Disease) (Genetic Disorders) - Drugs in Development, 2021 Summary Subacute Necrotizing Encephalomyelopathy (Leigh Disease) (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Subacute Necrotizing Encephalomyelopathy (Leigh Disease)...

  • Genetic Disorder
  • World

Netherton Syndrome (Trichorrhexis Invaginata, Bamboo Hair) (Genetic Disorders) - Drugs in Development, 2021 Summary Netherton Syndrome (Trichorrhexis Invaginata, Bamboo Hair) (Genetic Disorders) - Drugs in Development, 2021 provides an overview of the Netherton Syndrome (Trichorrhexis Invaginata,...

  • Genetic Disorder
  • World