Global Metachromatic Leukodystrophy Drug Pipeline Trends 2019: Discovery, Pre-clinical, Clinical, In Approval Therapeutics, Companies and Markets

Global Metachromatic Leukodystrophy Drug Pipeline Trends 2019: Discovery, Pre-clinical, Clinical, In Approval Therapeutics, Companies and Markets

  • August 2019 •
  • 43 pages •
  • Report ID: 5811385 •
  • Format: PDF
High levels of pipeline activity are being observed in Metachromatic Leukodystrophy treatment during 2019. Clinical development activities are being undertaken by more than 10 companies including ArmaGen Inc, Homology Medicines Inc, Recursion Pharmaceuticals Inc, RegenxBio Inc, Takeda Pharmaceutical Company Ltd and others.

A Significant contribution to the Metachromatic Leukodystrophy pipeline is being observed from emerging companies opting for new approaches to clinical development strategy. The early stage and late-stage Metachromatic Leukodystrophy pipeline included 7 compounds, driven by increasing number of targeted therapies. Progress is being made in accelerating compounds into advanced stages. However, fluctuating trends are being observed in average duration across three phases.

Increased understanding of underlying causes of Metachromatic Leukodystrophy condition and increased access to investments is encouraging growth of Metachromatic Leukodystrophy drug pipeline. However, despite high levels of pipeline activity, increasing clinical trial costs and decreasing drug approval rates is requiring companies to focus more on understanding clinical development pipeline compounds.

The research study is structured to provide clear and actionable insights into Metachromatic Leukodystrophy drug pipeline for companies to optimize spending levels by understanding competition, their pipeline products and prospect of further advances over the next few years.

The report addresses the discovery, research and pre-clinical stage active Metachromatic Leukodystrophy therapeutic candidates. Further, drugs in clinical stage including phase 1, phase 2, phase 3 and pre-registration phases are also analyzed.

The current report examines the current Metachromatic Leukodystrophy pipeline along with current development status, regulatory progress, mechanism of action, route of administration, collaborating companies, sponsors, molecule type, and research/discovery details.

In addition to drug overview, recent developments, the report also provides mechanism of action, Pre-clinical trial details and Clinical trial details for each of the drug candidates of Metachromatic Leukodystrophy. Further, orphan drug status, fast track designation, grants awarded and other special status for Metachromatic Leukodystrophy pipeline compounds are also included.
This study was produced independently by VPAResearch from our proprietary databases, primarily to assist users to develop in-depth understanding of 2019 Metachromatic Leukodystrophy pipeline and formulate effective research and development strategies.

Research Methodology
Our integrated data reports are built through robust research methodology to ensure our users can build on the insights and data accuracy for their expansion plans. Both primary and secondary research methods are used with stringent quality checks at each stage to evaluate trends, analysis and forecasts.

Scope of the Research

Metachromatic Leukodystrophy Pipeline candidates-
- Pre-clinical Phase: Discovery, research, pre-clinical
- Early Phase: Phase 1 and Phase 2 Metachromatic Leukodystrophy drugs
- Late phase: Phase 3 and in-approval Metachromatic Leukodystrophy drugs

Companies involved in the Pipeline-
- Company overview
- Snapshot
- Metachromatic Leukodystrophy therapeutic treatment activities

Details for each Metachromatic Leukodystrophy drug candidate-
- Snapshot
- Drug Name
- Alternative Names
- Company
- Originator
- Phase
- Molecule Type
- Orphan Drug Status
- Drug Overview
- Mechanism of Action
- Current Status
- Trial Details

Other details
- Pre-clinical trials for each drug candidate
- Clinical trials for each drug candidate

Recent Metachromatic Leukodystrophy therapeutic candidates, clinical trials, investments, grants, partnerships, licenses, awards and other news