2 reports

  • GENE THERAPY PIPELINE CANDIDATES BY COMPANY

It is a gene therapy candidate that involves a one-time intravenous infusion of SPK-##.

  • Blood Disease
  • Gene Therapy
  • Pharmaceutical
  • Therapy
  • Alnylam Pharmaceuticals, Inc.

DEC ##, 2017: ONE-DOSE GENE THERAPY PRODUCES CLOTTING FACTOR, SAFELY STOPS BLEEDING IN HEMOPHILIA B PATIENTS A team of gene therapy researchers has reported positive results in a phase ##/ ## clinical trial for the inherited bleeding disorder hemophilia B.

  • Blood Disease
  • Gene Therapy
  • Protein Therapy
  • Therapy
  • Alnylam Pharmaceuticals, Inc.